United Kingdom Genetic Disorder Drugs Research

18 comprehensive market analysis studies and research reports on the United Kingdom Genetic Disorder Drugs sector, offering an overview with historical data since 2019 and forecasts up to 2030. This includes a detailed market research of 224 companies, enriched with industry statistics, insights, and a lot more.

Uk Genetic Disorder Drugs Industry Mordor Intelligence

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18 Healthcare Reports
Duchenne Muscular Dystrophy Treatment Market Major Players
Duchenne Muscular Dystrophy Treatment Market
CAGR: 19.08%
Study Period: 2019 - 2030
Country Covered: United Kingdom
Major Players:NIPPON SHINYAKU CO., LTD. (NS Pharma Inc.), ITALFARMACO S.p.A., PTC Therapeutics, Santhera Pharmaceuticals, Sarepta Therapeutics
Hereditary Angioedema Therapeutics Market Major Players
Hereditary Angioedema Therapeutics Market
CAGR: 16.90%
Study Period: 2019 - 2030
Country Covered: United Kingdom
Major Players:Takeda Pharmaceuticals, CSL Behring, Pharming Group NV, BioCryst Pharmaceuticals, KalVista Pharmaceuticals
Monogenetic Disease Therapy Market Major Players
Monogenetic Disease Therapy Market
CAGR: 10.80%
Study Period: 2020 - 2030
Country Covered: United Kingdom
Major Players:Bayer, Novartis, Pfizer, Sanofi, Bluebird Bio
Vitiligo Treatment Market Major Players
Vitiligo Treatment Market
CAGR: 6.14%
Study Period: 2019 - 2030
Country Covered: United Kingdom
Major Players:Abbvie, Pfizer, Incyte, STRATA Skin Sciences Inc., Merck
Transthyretin Amyloidosis Treatment Market Major Players
Transthyretin Amyloidosis Treatment Market
CAGR: 15.40%
Study Period: 2019 - 2030
Country Covered: United Kingdom
Major Players:Pfizer, Alnylam Pharmaceuticals, Intellia Therapeutics, Inc., AstraZeneca, BridgeBio Pharma Inc
Fabry Disease Treatment Market Major Players
Fabry Disease Treatment Market
CAGR: 7.74%
Study Period: 2019 - 2030
Country Covered: United Kingdom
Major Players:Sanofi, Takeda Pharmaceuticals, Amicus Therapeutics, ISU ABXIS, JCR Pharmaceuticals
DNA Repair Drugs Market Major Players
DNA Repair Drugs Market
CAGR: 13.20%
Study Period: 2019 - 2030
Country Covered: United Kingdom
Major Players:AstraZeneca, GlaxoSmithKline, Merck, Pfizer, Valerio Therapeutics
Huntington's Disease Treatment Market Major Players
Huntington's Disease Treatment Market
CAGR: 8.23%
Study Period: 2019 - 2030
Country Covered: United Kingdom
Major Players:Pfizer, Alnylam Pharmaceuticals, Teva Pharmaceutical Industries, Neurocrine Biosciences, Ionis Pharmaceuticals
Sickle Cell Treatment Market Major Players
Sickle Cell Treatment Market
CAGR: 14.98%
Study Period: 2019 - 2030
Country Covered: United Kingdom
Major Players:Novartis, Sanofi, Pfizer, Vertex Pharmaceuticals Inc., CRISPR Therapeutics AG
Pompe Disease Market Major Players
Pompe Disease Market
CAGR: 7.32%
Study Period: 2019 - 2030
Country Covered: United Kingdom
Major Players:Amicus Therapeutics, Sanofi, Exerkine Corporation, Genethon, Maze Therapeutics, Inc.
Hunter Syndrome Treatment Market Major Players
Hunter Syndrome Treatment Market
CAGR: 5.30%
Study Period: 2021 - 2030
Country Covered: United Kingdom
Major Players:REGENXBIO, Clinigen Group, JCR Pharmaceuticals, ArmaGen, Takeda Pharmaceuticals
NTRK Fusion Gene Positive Advanced Solid Tumor Market Major Players
NTRK Fusion Gene Positive Advanced Solid Tumor Market
CAGR: 5.41%
Study Period: 2019 - 2030
Country Covered: United Kingdom
Major Players:Bayer, Empire Genomics, Roche, NeoGenomics Laboratories, OncoDNA S.A.
Cystic Fibrosis Therapeutics Market Major Players
Cystic Fibrosis Therapeutics Market
CAGR: 11.86%
Study Period: 2019 - 2030
Country Covered: United Kingdom
Major Players:Abbvie, Gilead Sciences, Vertex Pharmaceuticals Inc., Alaxia SAS, Mylan NV (Viatris)
Hemoglobinopathies Treatment Market Major Players
Hemoglobinopathies Treatment Market
CAGR: 7.98%
Study Period: 2019 - 2030
Country Covered: United Kingdom
Major Players:Sanofi, Novartis, Pfizer, bluebird bio, CSL Behring
Thalassemia Treatment Market Major Players
Thalassemia Treatment Market
CAGR: 3.76%
Study Period: 2019 - 2030
Country Covered: United Kingdom
Major Players:Bluebird Bio, Novartis, ApoPharma, Bellicum Pharmaceuticals, Pfizer
Global Rare Hemophilia Factors Market Major Players
Global Rare Hemophilia Factors Market
CAGR: 4.3%
Study Period: 2019 - 2030
Country Covered: United Kingdom
Major Players:Bayer, Pfizer, Takeda Pharmaceuticals, Sanofi, Novo Nordisk
Von Willebrand Disease Treatment Market Major Players
Von Willebrand Disease Treatment Market
CAGR: 6.5%
Study Period: 2019 - 2030
Country Covered: United Kingdom
Major Players:CSL Behring, Grifols, Octapharma, Bio Products Laboratory, Takeda (Shire)
Hemophilia Market Major Players
Hemophilia Market
CAGR: 5.74%
Study Period: 2019 - 2030
Country Covered: United Kingdom
Major Players:Biomarin Pharmaceutical, CSL Behring, Roche, Novo Nordisk, Pfizer
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