Rare Disease Drugs Research

12 comprehensive market analysis studies and research reports on the Rare Disease Drugs sector, offering an overview with historical data since 2019 and forecasts up to 2030. This includes a detailed market research of 123 companies, enriched with industry statistics, insights, and a lot more.

Rare Disease Drugs Industry Mordor Intelligence

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12 Healthcare Reports
United States Ultomiris Drug Market Major Players
United States Ultomiris Drug Market
CAGR: 23.45%
Study Period: 2020 - 2031
Country Covered: United States
Major Players:AstraZeneca
Neurotrophic Keratitis Treatment Market Major Players
Neurotrophic Keratitis Treatment Market
CAGR: 5.58%
Study Period: 2020 - 2031
Regions Covered: North America, Europe, Asia Pacific, Middle East and Africa, South America
Major Players:Dompé farmaceutici S.p.A., Bausch + Lomb, Laboratoires Théa, RegeneRx Biopharmaceuticals, Inc., AxoGen, Inc
Bullous Pemphigoid Market Major Players
Bullous Pemphigoid Market
CAGR: 9.80%
Study Period: 2020 - 2031
Regions Covered: North America, Europe, Asia Pacific, Middle East and Africa, South America
Major Players:Abbvie, Bristol-Myers Squibb, Regeneron Pharmaceuticals, Sanofi, UCB
Alpha Mannosidosis Market Major Players
Alpha Mannosidosis Market
CAGR: 16.40%
Study Period: 2019 - 2030
Regions Covered: North America, Europe, Asia-Pacific, Middle East and Africa, South America
Major Players:Chiesi Farmaceutici, Sobi, Orchard Therapeutics plc, Avrobio, Ultragenyx Pharmaceutical Inc.
Hypoparathyroidism Treatment Market Major Players
Hypoparathyroidism Treatment Market
CAGR: 4%
Study Period: 2019 - 2030
Regions Covered: North America, Europe, Asia Pacific, Middle East and Africa, South America
Major Players:Roche, Teva Pharmaceutical Industries, Amgen, Zhejiang NHU, EnteraBio Ltd.
Monkeypox Vaccine and Treatment Market Major Players
Monkeypox Vaccine and Treatment Market
CAGR: 10.1%
Study Period: 2021 - 2030
Regions Covered: North America, Europe, Asia-Pacific, Middle East and Africa, South America
Major Players:Bavarian Nordic, SIGA Technologies, Chimerix
Neuromyelitis Optica Spectrum Disorder Market Major Players
Neuromyelitis Optica Spectrum Disorder Market
CAGR: 6.31%
Study Period: 2019 - 2030
Regions Covered: North America, Europe, Asia Pacific
Major Players:Roche, TG Therapeutics, Opexa Therapeutics, Mitsubishi Tanabe Pharma, Horizon Therapeutics
Rare Disease Treatment Market Major Players
Rare Disease Treatment Market
CAGR: 11.78%
Study Period: 2020 - 2031
Regions Covered: North America, Europe, Asia Pacific, South America, Middle East and Africa
Major Players:Amgen, Biomarin Pharmaceutical, Bayer, Bristol-Myers Squibb, AstraZeneca
Rare Neurological Disease Treatment Market Major Players
Rare Neurological Disease Treatment Market
CAGR: 6.66%
Study Period: 2022 - 2031
Regions Covered: North America, Europe, Asia Pacific, South America, Middle East and Africa
Major Players:CSL Behring, Merz Pharma, Kedrion Biopharma, US WorldMeds, Aquestive Therapeutics
Guillain-Barre Syndrome Market Major Players
Guillain-Barre Syndrome Market
CAGR: 5.7%
Study Period: 2020 - 2031
Regions Covered: North America, Europe, Asia Pacific, Middle East and Africa, South America
Major Players:CSL Behring, Takeda Pharmaceuticals, Grifols, Kedrion Biopharma, Octapharma
Scleroderma Therapeutics Market Major Players
Scleroderma Therapeutics Market
CAGR: 7.68%
Study Period: 2020 - 2031
Regions Covered: North America, Europe, Asia-Pacific, Middle East and Africa, South America
Major Players:Boehringer Ingelheim, Roche, Johnson & Johnson Services Inc. (Actelion), Bayer, Novartis
Orphan Drugs Market Major Players
Orphan Drugs Market
CAGR: 6.36%
Study Period: 2020 - 2031
Regions Covered: North America, Europe, Asia Pacific, Middle East and Africa, South America
Major Players:Novartis, Roche, Abbvie, Sanofi, Pfizer
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