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14 Genetic Disorder Drugs Reports

Cystic Fibrosis (CF) Therapeutics Market

Study Period: 2019 - 2029

Regions Covered: North America, Europe, Asia-Pacific, Middle East and Africa, South America

Major Players: AbbVie Inc , Gilead Sciences, Inc, Mylan N.V, Alaxia, Vertex Pharmaceuticals Incorporated

Pompe Disease Market

Study Period: 2019 - 2029

Regions Covered: North America, Europe, Asia-Pacific, Middle East and Africa, South America

Major Players: Amicus Therapeutics, EpiVax, Inc, Sanofi Inc., AVROBIO, Inc., Astellas Pharma

Hemophilia Factors Market

Study Period: 2019 - 2029

Regions Covered: North America, Europe, Asia Pacific, Middle East and Africa, South America

Major Players: Bayer AG, Pfizer, Inc., Takeda Pharmaceutical Co. Ltd., Sanofi S.A, Novo Nordisk

Hemophilia Market

Study Period: 2019 - 2029

Regions Covered: North America, Europe, Asia Pacific, Middle East and Africa, South America

Major Players: Pfizer, Inc., Bayer AG, Novo Nordisk A/S, CSL Limited (CSL Behring), BioMarin

Duchenne Muscular Dystrophy Treatment Market

Study Period: 2019 - 2029

Regions Covered: North America, Europe, Asia Pacific, Asia Pacific

Major Players: Pfizer Inc., Sarepta Therapeutics, PTC Therapeutics, FibroGen Inc., F. Hoffmann-La Roche AG

Thalassemia Treatment Market

Study Period: 2019 - 2029

Regions Covered: North America, Europe, Asia-Pacific, Middle East and Africa, South America

Major Players: Bluebird Bio, Novartis AG, ApoPharma Inc, Bellicum Pharmaceuticals, Pfizer, Inc.

Von Willebrand Disease Treatment Market

Study Period: 2019 - 2029

Regions Covered: North America, Europe, Asia Pacific, Middle East and Africa, South America

Major Players: CSL Behring, Grifols, S.A., Takeda Pharmaceutical Company Ltd, Octapharma AG, Bio Products Laboratory Ltd.

Hereditary Angioedema Treatment Market

Study Period: 2019 - 2029

Regions Covered: North America, Europe, Asia-Pacific, Middle East and Africa, South America

Major Players: CSL Behring, Takeda Pharmaceutical Company Limited, Pharming Healthcare Inc., Sanofi, BioCryst Pharmaceuticals Inc.

Sickle Cell Treatment Industry

Study Period: 2019 - 2029

Regions Covered: North America, Europe, Asia-Pacific, Middle East and Africa, South America

Major Players: Novartis AG, Emmaus Medical Inc., Addmedica, Medunik USA Inc., Global Blood Therapeutics Inc

DNA Repair Drugs Market

Study Period: 2019 - 2029

Regions Covered: North America, Europe, Asia-Pacific

Major Players: AstraZeneca plc, Clovis Oncology, GlaxoSmithKline plc., Pfizer Inc., Onxeo

Huntington's Disease Treatment Market

Study Period: 2019 - 2029

Regions Covered: North America, Europe, Asia-Pacific, Middle East and Africa, South America

Major Players: Pfizer, Inc., Alnylam Pharmaceuticals Inc., Teva Pharmaceutical Industries Ltd., Neurocrine Biosciences, Inc., Ionis Pharmaceuticals

Hunter Syndrome Treatment Market

Study Period: 2021 - 2029

Regions Covered: North America, Europe, Asia-Pacific

Major Players: REGENXBIO Inc., Clinigen Group plc, JCR Pharmaceuticals, ArmaGen, Takeda Pharmaceutical Company Limited (Shire)

Hemoglobinopathies Treatment Market

Study Period: 2019 - 2029

Regions Covered: North America, Europe, Asia-Pacific, Middle East and Africa, South America

Major Players: Sanofi S.A., Global Blood Therapeutics, Inc., bluebird bio, Inc., EMI Holding, Inc., Celgene Corporation

Fabry Disease Treatment Market

Study Period: 2019 - 2029

Regions Covered: North America, Europe, Asia Pacific

Major Players: Sanofi (Genzyme Corporation), Takeda Pharmaceutical Company Limited, Amicus Therapeutics, Inc, ISU ABXIS, JCR Pharmaceuticals Co., Ltd.

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