Orphan Drugs Top Companies
Takeda Pharmaceuticals
Novartis
Johnson & Johnson
Roche
Bristol-Myers Squibb
*Disclaimer: Top companies sorted in no particular order

Orphan Drugs Market Concentration

Orphan Drugs Company List
Johnson & Johnson
Novartis
Roche
Bristol-Myers Squibb
Amgen
Pfizer
Takeda Pharmaceuticals
Sanofi
AstraZeneca
Abbvie
Alexion Pharmaceuticals Inc.
GlaxoSmithKline
Daiichi Sankyo Co. Ltd
Bayer
Vertex Pharmaceuticals Inc.
Horizon Therapeutics
Regeneron Pharmaceuticals
Biomarin Pharmaceutical
CSL Behring
Sarepta Therapeutics


